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Drug makes cells ignore mutation

Experimental cystic-fibrosis treatment could be used in many diseases.

A drug that corrects the effects of a genetic mutation has produced encouraging results in tests on patients. The drug, PTC124, is designed to fool a patient's cells into producing a functional protein, even though that protein's gene is mutated.

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Is there a coresponding publication for this research? Is this somehow specific for one mRNA?...because ignoring stop codons non-specifically seems like a doomed approach...

interesting read.

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