Drug makes cells ignore mutation
Experimental cystic-fibrosis treatment could be used in many diseases.
A drug that corrects the effects of a genetic mutation has produced encouraging results in tests on patients. The drug, PTC124, is designed to fool a patient's cells into producing a functional protein, even though that protein's gene is mutated.
Read the story here.

Comments
Is there a coresponding publication for this research? Is this somehow specific for one mRNA?...because ignoring stop codons non-specifically seems like a doomed approach...
interesting read.
Posted by: Adam MacNeil | November 10, 2006 03:32 AM